Molecule Details
InChIKeyYFHRCLAKZBDRHN-MRXNPFEDSA-N
Canonical SMILESCC(C)(NC(=O)O[C@@H]1CN2CCC1CC2)c1csc(-c2ccc(F)cc2)n1
Clinical Status Data-mined Candidate
Targets (Human+Pathogen)2
Pfam Stratification Cross-Family
Avg pChEMBL7.01
SourceChEMBL;BindingDB
2D Structure
2D structure
Activity Profile
DrugBank Annotations
DrugBank ID DB14966
Drug NameVenglustat
CAS Number1401090-53-6
Groups investigational
ATC Codes nan
DescriptionVenglustat is under investigation in clinical trial NCT01674036 (Safety, Tolerability and Pharmacokinetics of Genz-682452 in Healthy Men).

Categories: Acids, Acyclic Enzyme Inhibitors
Cross-references: BindingDB: 50593123 CHEMBL4297611 ChemSpider: 34989426 PDB: KYF ZINC: ZINC000202143443
Target Activities (2)
Target Gene Organism Category Pfam pChEMBL Type Source
Q16739 UGCG Homo sapiens Human PF13506 7.6 IC50 ChEMBL;BindingDB
Q9BV86 NTMT1 Homo sapiens Human PF05891 6.4 IC50 ChEMBL;BindingDB
DrugBank Target Actions (1)
Target Gene Target Name Action Type
Q16739 UGCG Ceramide glucosyltransferase inhibitor targets