InChIKey	UQRORFVVSGFNRO-UTINFBMNSA-N
Compound Name	Miglustat
Canonical SMILES	CCCCN1C[C@H](O)[C@@H](O)[C@H](O)[C@H]1CO
Clinical Status	Data-mined Candidate
Targets (Human+Pathogen)	3
Pfam Stratification	Cross-Family
Avg pChEMBL	6.65
Source	ChEMBL;BindingDB

DrugBank ID	DB00419
Drug Name	Miglustat
CAS Number	72599-27-0
Groups	approved investigational
ATC Codes	A16AX06
Description	Miglustat, commonly marketed under the trade name Zavesca, is a drug used to treat Gaucher disease. It inhibits the enzyme glucosylceramide synthase, an essential enzyme for the synthesis of most glycosphingolipids. It is only used for patients who cannot be treated with enzyme replacement therapy w...

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Categories: Alimentary Tract and Metabolism Alkaloids Anti-HIV Agents Anti-Infective Agents Carbohydrates Enzyme Inhibitors Enzyme Stabilizer Gaucher Disease Glucosylceramide Synthase Inhibitor Glucosylceramide Synthase Inhibitors Glycoside Hydrolase Inhibitors Imines Imino Pyranoses Imino Sugars Other Miscellaneous Therapeutic Agents Piperidines Various Alimentary Tract and Metabolism Products

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Cross-references: BindingDB: 18355 ChEBI: 50381 CHEMBL1029 ChemSpider: 46764 Drugs Product Database (DPD): 13313 D05032 PDB: NBV PharmGKB: PA10140 PubChem:51634 PubChem:46506350 RxCUI: 402316 Therapeutic Targets Database: DAP000609 Wikipedia: Miglustat ZINC: ZINC000003794711