Molecule Details
InChIKeyUJLAWZDWDVHWOW-YPMHNXCESA-N
Compound NameTofacitinib
Canonical SMILESC[C@@H]1CCN(C(=O)CC#N)C[C@@H]1N(C)c1ncnc2[nH]ccc12
Clinical Status Data-mined Candidate
Targets (Human+Pathogen)16
Pfam Stratification Cross-Family
Avg pChEMBL6.84
SourceChEMBL;BindingDB
2D Structure
2D structure
Activity Profile
DrugBank Annotations
DrugBank ID DB08895
Drug NameTofacitinib
CAS Number477600-75-2
Groups approved investigational
ATC Codes L04AF01
DescriptionTofacitinib is an inhibitor of Janus kinases, a group of intracellular enzymes involved in signalling pathways that affect hematopoiesis and immune cell function. It is approved by the FDA for treatment of moderate to severe rheumatoid arthritis that responds inadequately to methotrexate or in those...

Categories: Antineoplastic and Immunomodulating Agents Antirheumatic Agents Biologics for Rheumatoid Arthritis Treatment Bradycardia-Causing Agents Cytochrome P-450 CYP2C19 Substrates Cytochrome P-450 CYP3A Substrates Cytochrome P-450 CYP3A4 Substrates Cytochrome P-450 Substrates Disease-modifying Antirheumatic Agents Enzyme Inhibitors Immunosuppressive Agents Janus Kinase Inhibitor Janus Kinase Inhibitors Janus Kinases, antagonists & inhibitors Myelosuppressive Agents Protein Kinase Inhibitors Selective Immunosuppressants
Cross-references: BindingDB: 50193995 ChEBI: 71200 CHEMBL221959 ChemSpider: 8102425 Drugs Product Database (DPD): 22274 D09970 PDB: MI1 PubChem:9926791 PubChem:347827811 RxCUI: 1357536 Wikipedia: Tofacitinib ZINC: ZINC000003818808
Target Activities (16)
Target Gene Organism Category Pfam pChEMBL Type Source
P52333 JAK3 Homo sapiens Human PF18379 PF18377 PF17887 PF07714 PF21990 8.5 IC50 ChEMBL;BindingDB
Q9C098 DCLK3 Homo sapiens Human PF00069 8.3 Kd ChEMBL;BindingDB
O60674 JAK2 Homo sapiens Human PF18379 PF18377 PF17887 PF07714 PF21990 7.8 IC50 ChEMBL;BindingDB
P23458 JAK1 Homo sapiens Human PF18379 PF18377 PF17887 PF07714 PF21990 7.8 IC50 ChEMBL;BindingDB
P29597 TYK2 Homo sapiens Human PF18379 PF18377 PF17887 PF07714 PF21990 7.3 IC50 ChEMBL;BindingDB
Q16512 PKN1 Homo sapiens Human PF02185 PF00069 PF00433 6.7 Kd ChEMBL;BindingDB
O75116 ROCK2 Homo sapiens Human PF25346 PF00069 PF08912 6.4 Kd ChEMBL;BindingDB
Q9H093 NUAK2 Homo sapiens Human PF00069 6.4 Kd ChEMBL;BindingDB
Q02750 MAP2K1 Homo sapiens Human PF00069 6.4 Kd ChEMBL
P06239 LCK Homo sapiens Human PF07714 PF00017 PF00018 6.3 Kd ChEMBL;BindingDB
Q13464 ROCK1 Homo sapiens Human PF25346 PF00069 PF08912 6.3 Kd ChEMBL;BindingDB
Q96GD4 AURKB Homo sapiens Human PF00069 6.3 Kd ChEMBL
Q9UK32 RPS6KA6 Homo sapiens Human PF00069 PF00433 6.3 Kd ChEMBL;BindingDB
Q5S007 LRRK2 Homo sapiens Human PF23745 PF23744 PF23748 PF16095 PF25497 PF13855 PF00069 PF08477 6.3 Kd ChEMBL;BindingDB
Q15349 RPS6KA2 Homo sapiens Human PF00069 PF00433 6.2 Kd ChEMBL;BindingDB
Q13470 TNK1 Homo sapiens Human PF07714 PF22931 6.2 Kd ChEMBL;BindingDB
DrugBank Target Actions (7)
Target Gene Target Name Action Type
P02768 ALB Albumin binder carriers
P08684 CYP3A4 Cytochrome P450 3A4 substrate enzymes
P33261 CYP2C19 Cytochrome P450 2C19 substrate enzymes
O60674 JAK2 Tyrosine-protein kinase JAK2 inhibitor targets
P23458 JAK1 Tyrosine-protein kinase JAK1 inhibitor targets
P29597 TYK2 Non-receptor tyrosine-protein kinase TYK2 inhibitor targets
P52333 JAK3 Tyrosine-protein kinase JAK3 inhibitor targets