Molecule Details
InChIKeyPTOAARAWEBMLNO-KVQBGUIXSA-N
Compound NameCladribine
Canonical SMILESNc1nc(Cl)nc2c1ncn2[C@H]1C[C@H](O)[C@@H](CO)O1
Clinical Status Data-mined Candidate
Targets (Human+Pathogen)3
Pfam Stratification Cross-Family
Avg pChEMBL7.05
SourceBindingDB;ChEMBL
2D Structure
2D structure
Activity Profile
DrugBank Annotations
DrugBank ID DB00242
Drug NameCladribine
CAS Number4291-63-8
Groups approved investigational
ATC Codes L04AA40 L01BB04
DescriptionCladribine is a purine analogue or a chlorinated derivative of adenine [A263733] that causes apoptosis of B and T lymphocytes.[A350] Cladribine was first approved in the United States in 1993 [A263713] initially as a treatment for a number of hematological malignancies; currently, it is approved for...

Categories: 2-Chloroadenosine Agents Causing Muscle Toxicity Antimetabolites Antineoplastic Agents Antineoplastic and Immunomodulating Agents BCRP/ABCG2 Substrates Cardiotoxic antineoplastic agents Deoxyadenosines Deoxyribonucleosides Heterocyclic Compounds, Fused-Ring Immunologic Factors Immunosuppressive Agents Myelosuppressive Agents Nucleic Acids, Nucleotides, and Nucleosides Nucleosides P-glycoprotein substrates Purine Analogues Purine Antimetabolite Purine Nucleosides Purines Ribonucleosides Selective Immunosuppressants
Cross-references: BindingDB: 50008366 ChEBI: 567361 CHEMBL1619 ChemSpider: 19105 Drugs Product Database (DPD): 1739 D01370 PDB: CL9 PharmGKB: PA449027 PubChem:20279 PubChem:46504588 RxCUI: 44157 Therapeutic Targets Database: DAP000565 Wikipedia: Cladribine ZINC: ZINC000003798064
Target Activities (3)
Target Gene Organism Category Pfam pChEMBL Type Source
P00491 PNP Homo sapiens Human PF01048 8.6 Ki ChEMBL
Q13285 NR5A1 Homo sapiens Human PF00104 PF00105 6.3 IC50 BindingDB
P35398 RORA Homo sapiens Human PF00104 PF00105 6.2 IC50 BindingDB
DrugBank Target Actions (17)
Target Gene Target Name Action Type
P27707 DCK Deoxycytidine kinase substrate enzymes
Q16854 Q16854 Deoxyguanosine kinase, mitochondrial substrate enzymes
P00491 PNP Purine nucleoside phosphorylase inducer targets
P09874 PARP1 Poly [ADP-ribose] polymerase 1 inducer targets
P00813 ADA Adenosine deaminase inhibitor targets
P09884 POLA1 DNA polymerase alpha catalytic subunit inhibitor targets
P23921 RRM1 Ribonucleoside-diphosphate reductase large subunit inhibitor targets
P31350 RRM2 Ribonucleoside-diphosphate reductase subunit M2 inhibitor targets
P56282 P56282 DNA polymerase epsilon subunit 2 inhibitor targets
Q07864 Q07864 DNA polymerase epsilon catalytic subunit A inhibitor targets
Q7LG56 RRM2B Ribonucleoside-diphosphate reductase subunit M2 B inhibitor targets
Q9NR33 Q9NR33 DNA polymerase epsilon subunit 4 inhibitor targets
Q9NRF9 POLE3 DNA polymerase epsilon subunit 3 inhibitor targets
Q99808 SLC29A1 Equilibrative nucleoside transporter 1 binder transporters
P08183 ABCB1 ATP-dependent translocase ABCB1 substrate transporters
Q9HAS3 Q9HAS3 Solute carrier family 28 member 3 substrate transporters
Q9UNQ0 ABCG2 Broad substrate specificity ATP-binding cassette transporter ABCG2 substrate transporters