Molecule Details
InChIKeyPHXJVRSECIGDHY-UHFFFAOYSA-N
Compound NamePonatinib
Canonical SMILESCc1ccc(C(=O)Nc2ccc(CN3CCN(C)CC3)c(C(F)(F)F)c2)cc1C#Cc1cnc2cccnn12
Clinical Status Data-mined Candidate
Targets (Human+Pathogen)59
Pfam Stratification Cross-Family
Avg pChEMBL7.67
SourceBindingDB;ChEMBL
2D Structure
2D structure
Activity Profile
DrugBank Annotations
DrugBank ID DB08901
Drug NamePonatinib
CAS Number943319-70-8
Groups approved investigational
ATC Codes L01EA05
DescriptionPonatinib is a novel Bcr-Abl tyrosine kinase inhibitor that is especially effective against the T315I mutation for the treatment of chronic myeloid leukemia. FDA approved on December 14, 2012.

Categories: Antineoplastic Agents Antineoplastic and Immunomodulating Agents BCRP/ABCG2 Inhibitors BCRP/ABCG2 Substrates Bcr-Abl Tyrosine Kinase Inhibitors Cytochrome P-450 CYP2C8 Substrates Cytochrome P-450 CYP2C8 Substrates with a Narrow Therapeutic Index Cytochrome P-450 CYP2D6 Substrates Cytochrome P-450 CYP2D6 Substrates with a Narrow Therapeutic Index Cytochrome P-450 CYP3A Substrates Cytochrome P-450 CYP3A4 Substrates Cytochrome P-450 CYP3A4 Substrates with a Narrow Therapeutic Index Cytochrome P-450 CYP3A5 Substrates Cytochrome P-450 CYP3A5 Substrates with a Narrow Therapeutic Index Cytochrome P-450 Substrates Enzyme Inhibitors Hepatotoxic Agents Immunosuppressive Agents Kinase Inhibitor Myelosuppressive Agents Narrow Therapeutic Index Drugs P-glycoprotein inhibitors P-glycoprotein substrates P-glycoprotein substrates with a Narrow Therapeutic Index Protein Kinase Inhibitors Tyrosine Kinase Inhibitors
Cross-references: BindingDB: 50322535 ChEBI: 78543 CHEMBL1171837 ChemSpider: 24747381 Drugs Product Database (DPD): 22576 D09950 PDB: 0LI PharmGKB: PA165980594 PubChem:24826799 PubChem:175427142 RxCUI: 1364347 Wikipedia: Ponatinib ZINC: ZINC000036701290
Target Activities (59)
Target Gene Organism Category Pfam pChEMBL Type Source
P08631 HCK Homo sapiens Human PF07714 PF00017 PF00018 10.0 IC50 ChEMBL;BindingDB
P07948 LYN Homo sapiens Human PF07714 PF00017 PF00018 9.6 IC50 ChEMBL;BindingDB
P06239 LCK Homo sapiens Human PF07714 PF00017 PF00018 9.6 IC50 ChEMBL;BindingDB
P06241 FYN Homo sapiens Human PF07714 PF00017 PF00018 9.4 IC50 ChEMBL;BindingDB
P00519 ABL1 Homo sapiens Human PF08919 PF07714 PF00017 PF00018 9.1 IC50 ChEMBL;BindingDB
P07947 YES1 Homo sapiens Human PF07714 PF00017 PF00018 9.1 IC50 ChEMBL;BindingDB
P11274 BCR Homo sapiens Human PF09036 PF00168 PF19057 PF00620 PF00621 9.0 IC50 ChEMBL
P16234 PDGFRA Homo sapiens Human PF07679 PF25305 PF07714 9.0 IC50 ChEMBL;BindingDB
P09619 PDGFRB Homo sapiens Human PF00047 PF13927 PF25305 PF07714 8.9 IC50 ChEMBL;BindingDB
P42685 FRK Homo sapiens Human PF07714 PF00017 PF00018 8.9 IC50 ChEMBL;BindingDB
Q9Y572 RIPK3 Homo sapiens Human PF00069 PF12721 8.8 IC50 ChEMBL;BindingDB
P35968 KDR Homo sapiens Human PF07679 PF00047 PF13895 PF22971 PF07714 PF21339 PF17988 PF22854 8.8 IC50 ChEMBL;BindingDB
P11362 FGFR1 Homo sapiens Human PF07679 PF00047 PF07714 8.7 IC50 ChEMBL;BindingDB
P21802 FGFR2 Homo sapiens Human PF07679 PF13927 PF07714 8.7 IC50 ChEMBL;BindingDB
P12931 SRC Homo sapiens Human PF07714 PF00017 PF00018 8.3 IC50 ChEMBL;BindingDB
P10721 KIT Homo sapiens Human PF00047 PF07714 8.2 IC50 ChEMBL;BindingDB
O43353 RIPK2 Homo sapiens Human PF00619 PF07714 8.2 IC50 ChEMBL;BindingDB
P29317 EPHA2 Homo sapiens Human PF14575 PF25599 PF01404 PF00041 PF07714 PF00536 8.2 Kd ChEMBL;BindingDB
P22455 FGFR4 Homo sapiens Human PF07679 PF13927 PF07714 8.1 IC50 ChEMBL;BindingDB
P54756 EPHA5 Homo sapiens Human PF14575 PF25599 PF01404 PF00041 PF07714 PF00536 8.1 Kd ChEMBL
P07333 CSF1R Homo sapiens Human PF00047 PF25305 PF07714 8.1 IC50 ChEMBL;BindingDB
P17948 FLT1 Homo sapiens Human PF07679 PF00047 PF13927 PF22971 PF07714 PF21339 PF17988 PF22854 8.1 IC50 ChEMBL;BindingDB
P22607 FGFR3 Homo sapiens Human PF21165 PF07679 PF13927 PF07714 8.0 IC50 ChEMBL;BindingDB
Q08345 DDR1 Homo sapiens Human PF21114 PF00754 PF07714 8.0 IC50 ChEMBL;BindingDB
Q13546 RIPK1 Homo sapiens Human PF00531 PF07714 7.9 IC50 ChEMBL;BindingDB
P36888 FLT3 Homo sapiens Human PF00047 PF07714 7.9 IC50 ChEMBL;BindingDB
P41240 CSK Homo sapiens Human PF07714 PF00017 PF00018 7.9 IC50 ChEMBL;BindingDB
P15056 BRAF Homo sapiens Human PF00130 PF07714 PF02196 7.8 IC50 BindingDB
P49336 CDK8 Homo sapiens Human PF00069 7.8 IC50 ChEMBL
P42684 ABL2 Homo sapiens Human PF08919 PF07714 PF00017 PF00018 7.7 Kd ChEMBL
P07949 RET Homo sapiens Human PF00028 PF07714 PF17756 PF17812 PF17813 PF22540 7.6 IC50 ChEMBL;BindingDB
P04629 NTRK1 Homo sapiens Human PF13855 PF16920 PF07714 PF18613 7.5 IC50 ChEMBL
P23458 JAK1 Homo sapiens Human PF18379 PF18377 PF17887 PF07714 PF21990 7.5 IC50 ChEMBL;BindingDB
P09769 FGR Homo sapiens Human PF07714 PF00017 PF00018 7.4 Kd ChEMBL
Q9UNQ0 ABCG2 Homo sapiens Human PF01061 PF19055 PF00005 7.4 IC50 ChEMBL;BindingDB
Q12851 MAP4K2 Homo sapiens Human PF00780 PF00069 7.4 Kd ChEMBL
Q9NYL2 MAP3K20 Homo sapiens Human PF07714 PF07647 7.4 Kd ChEMBL
Q9NWZ3 IRAK4 Homo sapiens Human PF07714 7.2 IC50 ChEMBL
Q13470 TNK1 Homo sapiens Human PF07714 PF22931 7.1 Kd ChEMBL
Q92499 DDX1 Homo sapiens Human PF00270 PF00271 PF00622 7.1 Kd ChEMBL
Q16832 DDR2 Homo sapiens Human PF21114 PF00754 PF07714 7.1 Kd ChEMBL
Q15746 MYLK Homo sapiens Human PF16620 PF00041 PF07679 PF00069 7.0 Kd ChEMBL
P21709 EPHA1 Homo sapiens Human PF14575 PF25599 PF01404 PF07699 PF00041 PF07714 PF00536 6.8 IC50 ChEMBL;BindingDB
Q16539 MAPK14 Homo sapiens Human PF00069 6.8 Kd ChEMBL
O60674 JAK2 Homo sapiens Human PF18379 PF18377 PF17887 PF07714 PF21990 6.8 IC50 ChEMBL;BindingDB
Q16204 CCDC6 Homo sapiens Human PF09755 6.7 IC50 ChEMBL
Q5S007 LRRK2 Homo sapiens Human PF23745 PF23744 PF23748 PF16095 PF25497 PF13855 PF00069 PF08477 6.7 IC50 ChEMBL;BindingDB
Q14289 PTK2B Homo sapiens Human PF21477 PF00373 PF18038 PF03623 PF07714 6.5 Kd ChEMBL
O95819 MAP4K4 Homo sapiens Human PF00780 PF00069 6.5 Kd ChEMBL
Q00537 CDK17 Homo sapiens Human PF00069 6.5 Kd ChEMBL
Q9UKE5 TNIK Homo sapiens Human PF00780 PF00069 6.4 Kd ChEMBL
P49137 MAPKAPK2 Homo sapiens Human PF00069 6.3 Kd ChEMBL
Q13233 MAP3K1 Homo sapiens Human PF21040 PF00069 PF04434 6.3 Kd ChEMBL
P54753 EPHB3 Homo sapiens Human PF14575 PF25599 PF01404 PF07699 PF00041 PF07714 PF00536 6.3 Kd ChEMBL
P17612 PRKACA Homo sapiens Human PF00069 6.2 IC50 ChEMBL;BindingDB
P51617 IRAK1 Homo sapiens Human PF00531 PF00069 6.2 Kd ChEMBL
Q12809 KCNH2 Homo sapiens Human PF00027 PF00520 PF13426 6.1 IC50 ChEMBL;BindingDB
Q92918 MAP4K1 Homo sapiens Human PF00780 PF00069 6.1 Kd ChEMBL
Q15759 MAPK11 Homo sapiens Human PF00069 6.0 Kd ChEMBL
DrugBank Target Actions (23)
Target Gene Target Name Action Type
P08684 CYP3A4 Cytochrome P450 3A4 substrate enzymes
P10632 CYP2C8 Cytochrome P450 2C8 substrate enzymes
P10635 CYP2D6 Cytochrome P450 2D6 substrate enzymes
P20815 CYP3A5 Cytochrome P450 3A5 substrate enzymes
P00519 ABL1 Tyrosine-protein kinase ABL1 inhibitor targets
P06239 LCK Tyrosine-protein kinase Lck inhibitor targets
P07948 LYN Tyrosine-protein kinase Lyn inhibitor targets
P07949 RET Proto-oncogene tyrosine-protein kinase receptor Ret inhibitor targets
P10721 KIT Mast/stem cell growth factor receptor Kit inhibitor targets
P11274 BCR Breakpoint cluster region protein inhibitor targets
P11362 FGFR1 Fibroblast growth factor receptor 1 inhibitor targets
P12931 SRC Proto-oncogene tyrosine-protein kinase Src inhibitor targets
P16234 PDGFRA Platelet-derived growth factor receptor alpha inhibitor targets
P21802 FGFR2 Fibroblast growth factor receptor 2 inhibitor targets
P22455 FGFR4 Fibroblast growth factor receptor 4 inhibitor targets
P22607 FGFR3 Fibroblast growth factor receptor 3 inhibitor targets
P35968 KDR Vascular endothelial growth factor receptor 2 inhibitor targets
P36888 FLT3 Receptor-type tyrosine-protein kinase FLT3 inhibitor targets
Q02763 TEK Angiopoietin-1 receptor inhibitor targets
P08183 ABCB1 ATP-dependent translocase ABCB1 inhibitor transporters
Q9UNQ0 ABCG2 Broad substrate specificity ATP-binding cassette transporter ABCG2 inhibitor transporters
P08183 ABCB1 ATP-dependent translocase ABCB1 substrate transporters
Q9UNQ0 ABCG2 Broad substrate specificity ATP-binding cassette transporter ABCG2 substrate transporters