Molecule Details
InChIKeyPGTVWKLGGCQMBR-FLBATMFCSA-N
Compound NameGanaxolone
Canonical SMILESCC(=O)[C@H]1CC[C@H]2[C@@H]3CC[C@H]4C[C@](C)(O)CC[C@]4(C)[C@H]3CC[C@]12C
Clinical Status Data-mined Candidate
Targets (Human+Pathogen)16
Pfam Stratification Homologous
Avg pChEMBL6.74
SourceChEMBL
2D Structure
2D structure
Activity Profile
DrugBank Annotations
DrugBank ID DB05087
Drug NameGanaxolone
CAS Number38398-32-2
Groups approved investigational
ATC Codes N03AX27
DescriptionGanaxolone is the 3β-methylated synthetic analog of [allopregnanolone],[L41130] a metabolite of [progesterone].[A3197] Ganaxolone belongs to a class of compounds referred to as neurosteroids.[A3197] Endogenous neurosteroids, which comprise certain metabolites of progesterone and deoxycorticosterone,...

Categories: Anticonvulsants Central Nervous System Depressants Cytochrome P-450 CYP2B6 Substrates Cytochrome P-450 CYP2C19 Substrates Cytochrome P-450 CYP2D6 Substrates Cytochrome P-450 CYP3A Substrates Cytochrome P-450 CYP3A4 Substrates Cytochrome P-450 CYP3A5 Substrates Cytochrome P-450 Substrates Fused-Ring Compounds GABA Agents GABA Modulators Nervous System Neuroactive Steroid Gamma-Aminobutyric Acid A Receptor Positive Modulator Neurotransmitter Agents Pregnanes Steroids
Cross-references: BindingDB: 50369240 ChEBI: 177658 CHEMBL1568698 ChemSpider: 5293511 PharmGKB: PA166278301 PubChem:6918305 PubChem:175426940 RxCUI: 2604689 Wikipedia: Ganaxolone ZINC: ZINC000003824281
Target Activities (16)
Target Gene Organism Category Pfam pChEMBL Type Source
O00591 GABRP Homo sapiens Human PF02931 PF02932 6.7 IC50 ChEMBL
O14764 GABRD Homo sapiens Human PF02931 PF02932 6.7 IC50 ChEMBL
P14867 GABRA1 Homo sapiens Human PF02931 PF02932 6.7 IC50 ChEMBL
P18505 GABRB1 Homo sapiens Human PF02931 PF02932 6.7 IC50 ChEMBL
P18507 GABRG2 Homo sapiens Human PF02931 PF02932 6.7 IC50 ChEMBL
P28472 GABRB3 Homo sapiens Human PF02931 PF02932 6.7 IC50 ChEMBL
P31644 GABRA5 Homo sapiens Human PF02931 PF02932 6.7 IC50 ChEMBL
P34903 GABRA3 Homo sapiens Human PF02931 PF02932 6.7 IC50 ChEMBL
P47869 GABRA2 Homo sapiens Human PF02931 PF02932 6.7 IC50 ChEMBL
P47870 GABRB2 Homo sapiens Human PF02931 PF02932 6.7 IC50 ChEMBL
P48169 GABRA4 Homo sapiens Human PF02931 PF02932 6.7 IC50 ChEMBL
P78334 GABRE Homo sapiens Human PF02931 PF02932 6.7 IC50 ChEMBL
Q16445 GABRA6 Homo sapiens Human PF02931 PF02932 6.7 IC50 ChEMBL
Q8N1C3 GABRG1 Homo sapiens Human PF02931 PF02932 6.7 IC50 ChEMBL
Q99928 GABRG3 Homo sapiens Human PF02931 PF02932 6.7 IC50 ChEMBL
Q9UN88 GABRQ Homo sapiens Human PF02931 PF02932 6.7 IC50 ChEMBL
DrugBank Target Actions (6)
Target Gene Target Name Action Type
P08684 CYP3A4 Cytochrome P450 3A4 substrate enzymes
P10635 CYP2D6 Cytochrome P450 2D6 substrate enzymes
P20813 CYP2B6 Cytochrome P450 2B6 substrate enzymes
P20815 CYP3A5 Cytochrome P450 3A5 substrate enzymes
P33261 CYP2C19 Cytochrome P450 2C19 substrate enzymes
P14867 GABRA1 GABA(A) Receptor positive allosteric modulator targets