Molecule Details
InChIKeyIWKXDMQDITUYRK-KUBHLMPHSA-N
Compound NameForodesine
Canonical SMILESO=c1[nH]cnc2c([C@@H]3N[C@H](CO)[C@@H](O)[C@H]3O)c[nH]c12
Clinical Status Data-mined Candidate
Targets (Human+Pathogen)2
Pfam Stratification Homologous
Avg pChEMBL8.76
SourceChEMBL;BindingDB
2D Structure
2D structure
Activity Profile
DrugBank Annotations
DrugBank ID DB06185
Drug NameForodesine
CAS Number209799-67-7
Groups investigational
ATC Codes nan
DescriptionForodesine is a highly potent, orally active, rationally designed PNP inhibitor that has shown activity in preclinical studies with malignant cells and clinical utility against T-cell acute lymphoblastic leukemia and cutaneous T-cell lymphoma. Additional preliminary findings support its use for the ...

Categories: Heterocyclic Compounds, Fused-Ring Nucleic Acids, Nucleotides, and Nucleosides Nucleosides Purine-Nucleoside Phosphorylase, antagonists & inhibitors Purines Pyrimidines
Cross-references: BindingDB: 50195587 ChEBI: 43362 CHEMBL218291 ChemSpider: 392417 D06596 PDB: IMH PubChem:444499 Wikipedia: Forodesine ZINC: ZINC000013492899
Target Activities (2)
Target Gene Organism Category Pfam pChEMBL Type Source
P00491 PNP Homo sapiens Human PF01048 10.1 Ki ChEMBL;BindingDB
P9WP01 punA Mycobacterium tuberculosis (strain ATCC 25618 / H37Rv) Pathogen PF01048 7.4 IC50 ChEMBL
DrugBank Target Actions (1)
Target Gene Target Name Action Type
P00491 PNP Purine nucleoside phosphorylase inhibitor targets